1,6-epi-Cyclophellitol Cyclosulfamidate Is a Bona Fide Lysosomal α‑Glucosidase Stabilizer for the Treatment of Pompe Disease (English)
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In:
Journal of the American
Chemical Society
;
144
, 32
;
14819-14827
;
2022
- Article (Journal) / Electronic Resource
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Title:1,6-epi-Cyclophellitol Cyclosulfamidate Is a Bona Fide Lysosomal α‑Glucosidase Stabilizer for the Treatment of Pompe Disease
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Additional title:J. Am. Chem. Soc.
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Contributors:Kok, Ken ( author ) / Kuo, Chi-Lin ( author ) / Katzy, Rebecca E. ( author ) / Lelieveld, Lindsey T. ( author ) / Wu, Liang ( author ) / Roig-Zamboni, Véronique ( author ) / van der Marel, Gijsbert A. ( author ) / Codée, Jeroen D. C. ( author ) / Sulzenbacher, Gerlind ( author ) / Davies, Gideon J. ( author )
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Published in:Journal of the American Chemical Society ; 144, 32 ; 14819-14827
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Publisher:
- New search for: American Chemical Society
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Publication date:2022-08-17
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ISSN:
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Coden:
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DOI:
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Type of media:Article (Journal)
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Type of material:Electronic Resource
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Language:English
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Licence:
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Source:
Table of contents – Volume 144, Issue 32
The tables of contents are generated automatically and are based on the data records of the individual contributions available in the index of the TIB portal. The display of the Tables of Contents may therefore be incomplete.
- 14403
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Spotlights on Recent JACS PublicationsACS Contributing Correspondents et al. | 2022
- 14404
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Chemical and Enzymatic Methods for Post-Translational Protein–Protein ConjugationTaylor, Ross J. / Geeson, Michael B. / Journeaux, Toby / Bernardes, Gonçalo J. L. et al. | 2022
- 14420
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Luminescent and Photofunctional Transition Metal Complexes: From Molecular Design to Diagnostic and Therapeutic ApplicationsLee, Lawrence Cho-Cheung / Lo, Kenneth Kam-Wing et al. | 2022
- 14441
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Structural Studies of a Stapled Peptide with Native Ion Mobility-Mass Spectrometry and Transition Metal Ion Förster Resonance Energy Transfer in the Gas PhaseWu, Ri / Metternich, Jonas B. / Tiwari, Prince / Benzenberg, Lukas R. / Harrison, Julian A. / Liu, Qinlei / Zenobi, Renato et al. | 2022
- 14446
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Metal–Ligand–Anion Cooperation in C–H Bond Formation at Platinum(II)Zeitler, Hannah E. / Phearman, Alexander S. / Gau, Michael R. / Carroll, Patrick J. / Cundari, Thomas R. / Goldberg, Karen I. et al. | 2022
- 14452
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Photochemical Alkene Hydrophosphination with Bis(trichlorosilyl)phosphineGeeson, Michael B. / Tanaka, Keita / Taakili, Rachid / Benhida, Rachid / Cummins, Christopher C. et al. | 2022
- 14458
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Atroposelective Total Synthesis of Darobactin ALin, You-Chen / Schneider, Fabian / Eberle, Kelly J. / Chiodi, Debora / Nakamura, Hugh / Reisberg, Solomon H. / Chen, Jason / Saito, Masato / Baran, Phil S. et al. | 2022
- 14463
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C3-Selective Trifluoromethylthiolation and Difluoromethylthiolation of Pyridines and Pyridine Drugs via Dihydropyridine IntermediatesZhou, Xin-Yue / Zhang, Ming / Liu, Zhong / He, Jia-Hao / Wang, Xiao-Chen et al. | 2022
- 14471
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Efficient Synthesis of Orphaned Cyclopropanes Using Sulfones as Carbene EquivalentsJohnson, John Douglas / Teeples, Charles Reece / Akkawi, Nicholas Rajai / Wilkerson-Hill, Sidney M. et al. | 2022
- 14477
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Quantification of Excited-State Brønsted–Lowry Acidity of Weak Photoacids Using Steady-State Photoluminescence Spectroscopy and a Driving-Force-Dependent Kinetic TheoryBhide, Rohit / Feltenberger, Cassidy N. / Phun, Gabriel S. / Barton, Grant / Fishman, Dmitry / Ardo, Shane et al. | 2022
- 14489
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Mechanism of the Aryl–F Bond-Forming Step from Bi(V) FluoridesPlanas, Oriol / Peciukenas, Vytautas / Leutzsch, Markus / Nöthling, Nils / Pantazis, Dimitrios A. / Cornella, Josep et al. | 2022
- 14505
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Identification of the Highly Active Co–N4 Coordination Motif for Selective Oxygen Reduction to Hydrogen PeroxideChen, Shanyong / Luo, Tao / Li, Xiaoqing / Chen, Kejun / Fu, Junwei / Liu, Kang / Cai, Chao / Wang, Qiyou / Li, Hongmei / Chen, Yu et al. | 2022
- 14517
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Role of a “Magic” Methyl: 2′-Deoxy-2′-α-F-2′-β‑C‑methyl Pyrimidine Nucleotides Modulate RNA Interference Activity through Synergy with 5′-Phosphate Mimics and Mitigation of Off-Target EffectsGuenther, Dale C. / Mori, Shohei / Matsuda, Shigeo / Gilbert, Jason A. / Willoughby, Jennifer L. S. / Hyde, Sarah / Bisbe, Anna / Jiang, Yongfeng / Agarwal, Saket / Madaoui, Mimouna et al. | 2022
- 14535
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Chemical Synthesis of the Highly Sterically Hindered Core Undecasaccharide of Helicobacter pylori Lipopolysaccharide for Antigenicity Evaluation with Human SerumZou, Xiaopeng / Hu, Jing / Zhao, Ming / Qin, Chunjun / Zhu, Yuntao / Tian, Guangzong / Cai, Juntao / Seeberger, Peter H. / Yin, Jian et al. | 2022
- 14548
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Direct H2O2 Synthesis, without H2 GasHuang, Aoxue / Delima, Roxanna S. / Kim, Yongwook / Lees, Eric W. / Parlane, Fraser G. L. / Dvorak, David J. / Rooney, Michael B. / Jansonius, Ryan P. / Fink, Arthur G. / Zhang, Zishuai et al. | 2022
- 14555
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Enzyme-Catalyzed Spiroacetal Formation in Polyketide Antibiotic BiosynthesisBilyk, Oksana / Oliveira, Gabriel S. / de Angelo, Rafaela M. / Almeida, Michell O. / Honório, Kathia Maria / Leeper, Finian J. / Dias, Marcio V. B. / Leadlay, Peter F. et al. | 2022
- 14564
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The Single Residue K12 Governs the Exceptional Voltage Sensitivity of Mitochondrial Voltage-Dependent Anion Channel GatingNgo, Van A. / Queralt-Martín, María / Khan, Farha / Bergdoll, Lucie / Abramson, Jeff / Bezrukov, Sergey M. / Rostovtseva, Tatiana K. / Hoogerheide, David P. / Noskov, Sergei Yu. et al. | 2022
- 14578
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NEIL1 Recoding due to RNA Editing Impacts Lesion-Specific Recognition and ExcisionLotsof, Elizabeth R. / Krajewski, Allison E. / Anderson-Steele, Brittany / Rogers, JohnPatrick / Zhang, Lanxin / Yeo, Jongchan / Conlon, Savannah G. / Manlove, Amelia H. / Lee, Jeehiun K. / David, Sheila S. et al. | 2022
- 14590
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Fully Automated Unconstrained Analysis of High-Resolution Mass Spectrometry Data with Machine LearningBoiko, Daniil A. / Kozlov, Konstantin S. / Burykina, Julia V. / Ilyushenkova, Valentina V. / Ananikov, Valentine P. et al. | 2022
- 14607
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Valence-Inverted States of Nickel(II) Complexes Perform Facile C–H Bond ActivationWang, Shaohong / Ma, Pengchen / Shaik, Sason / Chen, Hui et al. | 2022
- 14614
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Tachykinin Neuropeptides and Amyloid β (25–35) Assembly: Friend or Foe?Liu, Xikun / Ganguly, Pritam / Jin, Yingying / Jhatro, Michael J. / Shea, Joan-Emma / Buratto, Steven K. / Bowers, Michael T. et al. | 2022
- 14627
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Identification of 7‑Deoxy-desulfo-argino-cylindrospermopsin, the Missing Piece in Cylindrospermopsin BiosynthesisMéjean, Annick / Lequin, Olivier / Ploux, Olivier et al. | 2022
- 14638
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Regulating Lithium Salt to Inhibit Surface Gelation on an Electrocatalyst for High-Energy-Density Lithium–Sulfur BatteriesLi, Xi-Yao / Feng, Shuai / Zhao, Chang-Xin / Cheng, Qian / Chen, Zi-Xian / Sun, Shu-Yu / Chen, Xiang / Zhang, Xue-Qiang / Li, Bo-Quan / Huang, Jia-Qi et al. | 2022
- 14647
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Live-Cell RNA Imaging with Metabolically Incorporated Fluorescent NucleosidesWang, Danyang / Shalamberidze, Ana / Arguello, A. Emilia / Purse, Byron W. / Kleiner, Ralph E. et al. | 2022
- 14657
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Deep Quantum-Dot Arrays in Moiré Superlattices of Non-van der Waals MaterialsSong, Zhigang / Wang, Yu / Zheng, Haimei / Narang, Prineha / Wang, Lin-Wang et al. | 2022
- 14668
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Deciphering the Folding Mechanism of Proteins G and L and Their MutantsChang, Liwei / Perez, Alberto et al. | 2022
- 14678
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Highly Stable and Selective Sensing of Hydrogen Sulfide in Living Mouse Brain with NiN4 Single-Atom Catalyst-Based Galvanic Redox PotentiometryPan, Cong / Wu, Fei / Mao, Junjie / Wu, Wenjie / Zhao, Gang / Ji, Wenliang / Ma, Wenjie / Yu, Ping / Mao, Lanqun et al. | 2022
- 14687
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Structure-Based Design of Stapled Peptides That Bind GABARAP and Inhibit AutophagyBrown, Hawley / Chung, Mia / Üffing, Alina / Batistatou, Nefeli / Tsang, Tiffany / Doskocil, Samantha / Mao, Weiqun / Willbold, Dieter / Bast, Robert C. / Lu, Zhen et al. | 2022
- 14698
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Growth Kinetics of Single Polymer Particles in Solution via Active-Feedback 3D TrackingYu, Donggeng / Garcia, Antonio / Blum, Suzanne A. / Welsher, Kevin D. et al. | 2022
- 14706
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Intrinsic and Extrinsic Limitations to the Design and Optimization of Inhibitors of Lipid Peroxidation and Associated Cell DeathFarmer, Luke A. / Wu, Zijun / Poon, Jia-Fei / Zilka, Omkar / Lorenz, Svenja M. / Huehn, Stephanie / Proneth, Bettina / Conrad, Marcus / Pratt, Derek A. et al. | 2022
- 14722
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Machine Learning Yield Prediction from NiCOlit, a Small-Size Literature Data Set of Nickel Catalyzed C–O CouplingsSchleinitz, Jules / Langevin, Maxime / Smail, Yanis / Wehnert, Benjamin / Grimaud, Laurence / Vuilleumier, Rodolphe et al. | 2022
- 14731
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Achieving Record-Efficiency Organic Solar Cells upon Tuning the Conformation of Solid AdditivesLi, Congqi / Gu, Xiaobin / Chen, Zhihao / Han, Xiao / Yu, Na / Wei, Yanan / Gao, Jinhua / Chen, Hao / Zhang, Meng / Wang, Ao et al. | 2022
- 14740
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Mechanistic Insights into Criegee Intermediate–Hydroperoxyl Radical ChemistryLi, Bai / Kumar, Manoj / Zhou, Chuan / Li, Lei / Francisco, Joseph S. et al. | 2022
- 14748
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Ligation Embedding Aggregation Disruptor Strategy Enables the Chemical Synthesis of PD‑1 Immunoglobulin and Extracellular DomainsWu, Hongxiang / Wei, Tongyao / Ngai, Wai Lok / Zhou, Haiyan / Li, Xuechen et al. | 2022
- 14758
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Copper-Catalyzed Glutathione Oxidation is Accelerated by the Anticancer Thiosemicarbazone Dp44mT and Further Boosted at Lower pHFalcone, Enrico / Ritacca, Alessandra G. / Hager, Sonja / Schueffl, Hemma / Vileno, Bertrand / El Khoury, Youssef / Hellwig, Petra / Kowol, Christian R. / Heffeter, Petra / Sicilia, Emilia et al. | 2022
- 14769
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Efficient Electrocatalytic Reduction of CO2 to Ethane over Nitrogen-Doped Fe2O3Chen, Peng / Zhang, Pei / Kang, Xinchen / Zheng, Lirong / Mo, Guang / Wu, Ruizhi / Tai, Jing / Han, Buxing et al. | 2022
- 14778
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Selective Potassium Chloride Recognition, Sensing, Extraction, and Transport Using a Chalcogen-Bonding Heteroditopic ReceptorDocker, Andrew / Marques, Igor / Kuhn, Heike / Zhang, Zongyao / Félix, Vítor / Beer, Paul D. et al. | 2022
- 14790
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Counterion-Mediated Enantioconvergent Synthesis of Axially Chiral Medium RingsDu, Ji-Yuan / Balan, Tudor / Claridge, Tim D. W. / Smith, Martin D. et al. | 2022
- 14798
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Step-Assisted On-Surface Synthesis of Graphene Nanoribbons Embedded with Periodic DivacanciesYin, Ruoting / Wang, Jianing / Qiu, Zhen-Lin / Meng, Jie / Xu, Huimin / Wang, Zhengya / Liang, Yifan / Zhao, Xin-Jing / Ma, Chuanxu / Tan, Yuan-Zhi et al. | 2022
- 14809
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Role of Electronic Structure on Nitrate Reduction to Ammonium: A Periodic JourneyCarvalho, O. Quinn / Marks, Rylee / Nguyen, Hoan K. K. / Vitale-Sullivan, Molly E. / Martinez, Selena C. / Árnadóttir, Líney / Stoerzinger, Kelsey A. et al. | 2022
- 14819
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1,6-epi-Cyclophellitol Cyclosulfamidate Is a Bona Fide Lysosomal α‑Glucosidase Stabilizer for the Treatment of Pompe DiseaseKok, Ken / Kuo, Chi-Lin / Katzy, Rebecca E. / Lelieveld, Lindsey T. / Wu, Liang / Roig-Zamboni, Véronique / van der Marel, Gijsbert A. / Codée, Jeroen D. C. / Sulzenbacher, Gerlind / Davies, Gideon J. et al. | 2022
- 14828
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Dealkenylative Alkynylation Using Catalytic FeII and Vitamin CSwain, Manisha / Bunnell, Thomas B. / Kim, Jacob / Kwon, Ohyun et al. | 2022
- 14838
-
Engineered Cytochrome P450-Catalyzed Oxidative Biaryl Coupling Reaction Provides a Scalable Entry into Arylomycin AntibioticsMolinaro, Carmela / Kawasaki, Yukie / Wanyoike, George / Nishioka, Taiki / Yamamoto, Tsuyoshi / Snedecor, Brad / Robinson, Sarah J. / Gosselin, Francis et al. | 2022
- 14846
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Ru-Catalyzed Hydroboration of Ynones Leads to a Nontraditional Mode of ReactivityFeng, Qiang / Li, Shijia / Li, Zhiyang / Yan, Qiaolin / Lin, Xiangfeng / Song, Lijuan / Zhang, Xinhao / Wu, Yun-Dong / Sun, Jianwei et al. | 2022
- 14856
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Catalytic Enantioselective α‑Alkylation of Amides by Unactivated Alkyl ElectrophilesTong, Xiaoyu / Schneck, Felix / Fu, Gregory C. et al. | 2022
- 14864
-
Atropisomeric Phosphine Ligands Bearing C–N Axial Chirality: Applications in Enantioselective Suzuki–Miyaura Cross-Coupling Towards the Assembly of Tetra-ortho-Substituted BiarylsGan, Kin Boon / Zhong, Rong-Lin / Zhang, Zhen-Wei / Kwong, Fuk Yee et al. | 2022
- 14874
-
Unraveling the Active Vanadium Sites and Adsorbate Dynamics in VO x /CeO2 Oxidation Catalysts Using Transient IR SpectroscopySchumacher, Leon / Weyel, Jakob / Hess, Christian et al. | 2022
- 14888
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Redox-Programmable Spin-Crossover Behaviors in a Cationic FrameworkWu, Si-Guo / Wang, Long-Fei / Ruan, Ze-Yu / Du, Shan-Nan / Gómez-Coca, Silvia / Ni, Zhao-Ping / Ruiz, Eliseo / Chen, Xiao-Ming / Tong, Ming-Liang et al. | 2022
- 14897
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Recognizing the Importance of Fast Nonisothermal Crystallization for High-Performance Two-Dimensional Dion–Jacobson Perovskite Solar Cells with High Fill Factors: A Comprehensive Mechanistic StudyLiu, Yi-Chun / Lin, Jin-Tai / Lee, Yao-Lin / Hung, Chieh-Ming / Chou, Tai-Che / Chao, Wei-Chih / Huang, Zhi-Xuan / Chiang, Tzu-Hsuan / Chiu, Ching-Wen / Chuang, Wei-Tsung et al. | 2022
- 14907
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Two-Dimensional Organic–Inorganic Room-Temperature MultiferroicsYang, Yali / Ji, Junyi / Feng, Junsheng / Chen, Shiyou / Bellaiche, Laurent / Xiang, Hongjun et al. | 2022
- 14915
-
Multistep Crystallization of Dynamic Nanoparticle Superlattices in Nonaqueous SolutionsZhong, Yaxu / Allen, Vincent R. / Chen, Jun / Wang, Yi / Ye, Xingchen et al. | 2022
- 14923
-
Switchable Radical Carbonylation by Philicity RegulationLu, Bin / Xu, Minghao / Qi, Xiaotian / Jiang, Min / Xiao, Wen-Jing / Chen, Jia-Rong et al. | 2022
- 14936
-
Electrocatalytic CO2‑to‑C2+ with Ampere-Level Current on Heteroatom-Engineered Copper via Tuning *CO Intermediate CoverageZheng, Min / Wang, Pengtang / Zhi, Xing / Yang, Kang / Jiao, Yan / Duan, Jingjing / Zheng, Yao / Qiao, Shi-Zhang et al. | 2022
- 14945
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Tracing of Acyl Carrier Protein-channeled Mitomycin Intermediates in Streptomyces caespitosus Facilitates Characterization of the Biosynthetic Steps for AHBA–GlcN Formation and ProcessingWang, Sili / Cheng, Yiyuan / Wang, Xiaofeng / Yang, Qian / Liu, Wen et al. | 2022
- 14957
-
Correction to “Mechanistic Insight into Copper-Mediated Trifluoromethylation of Aryl Halides: The Role of CuI”Liu, He / Wu, Jian / Jin, Yuxuan / Leng, Xuebing / Shen, Qilong et al. | 2022
- 14959
-
Correction to “Conformational Flexibility as a Tool for Enabling Site-Selective Functionalization of Unactivated sp 3 C–O Bonds in Cyclic Acetals”Romano, Ciro / Talavera, Laura / Gómez-Bengoa, Enrique / Martin, Ruben et al. | 2022