Progress in Rare Diseases Research 2010–2016: An IRDiRC Perspective (English)
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In:
Clinical and Translational Science
;
11
, 1
;
11-20
;
2018
- Article (Journal) / Electronic Resource
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Title:Progress in Rare Diseases Research 2010–2016: An IRDiRC Perspective
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Contributors:Dawkins, Hugh J.S. ( author ) / Draghia‐Akli, Ruxandra ( author ) / Lasko, Paul ( author ) / Lau, Lilian P.L. ( author ) / Jonker, Anneliene H. ( author ) / Cutillo, Christine M. ( author ) / Rath, Ana ( author ) / Boycott, Kym M. ( author ) / Baynam, Gareth ( author ) / Lochmüller, Hanns ( author )
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Published in:Clinical and Translational Science ; 11, 1 ; 11-20
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Publisher:
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Publication date:2018-01-01
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Size:10 pages
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ISSN:
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DOI:
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Type of media:Article (Journal)
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Type of material:Electronic Resource
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Language:English
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Source:
Table of contents – Volume 11, Issue 1
The tables of contents are generated automatically and are based on the data records of the individual contributions available in the index of the TIB portal. The display of the Tables of Contents may therefore be incomplete.
- 1
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Issue Information| 2018
- 4
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Know Your Variability: Challenges in Mechanistic Modeling of Inflammatory Response in Inflammatory Bowel Disease (IBD)Rogers, Katharine V. / Bhattacharya, Indranil / Martin, Steven W. / Nayak, Satyaprakash et al. | 2018
- 8
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Navigating the Clinical Translation of Medical Devices: The Case of Radiofrequency AblationArmaiz Flores, Abdel / Oppenheimer Velez, Marianna L. / Thompson, Scott M. / Windebank, Anthony J. / Greenberg‐Worisek, Alexandra J. et al. | 2018
- 11
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Progress in Rare Diseases Research 2010–2016: An IRDiRC PerspectiveDawkins, Hugh J.S. / Draghia‐Akli, Ruxandra / Lasko, Paul / Lau, Lilian P.L. / Jonker, Anneliene H. / Cutillo, Christine M. / Rath, Ana / Boycott, Kym M. / Baynam, Gareth / Lochmüller, Hanns et al. | 2018
- 21
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Future of Rare Diseases Research 2017–2027: An IRDiRC PerspectiveAustin, Christopher P. / Cutillo, Christine M. / Lau, Lilian P.L. / Jonker, Anneliene H. / Rath, Ana / Julkowska, Daria / Thomson, David / Terry, Sharon F. / de Montleau, Béatrice / Ardigò, Diego et al. | 2018
- 28
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Implementing the Single Institutional Review Board Model: Lessons from the Undiagnosed Diseases NetworkSplinter, Kimberly / Hull, Sara Chandros / Holm, Ingrid A. / McDonough, Tara L. / Wise, Anastasia L. / Ramoni, Rachel B. / Members of the Undiagnosed Diseases Network et al. | 2018
- 32
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Plasma Catechols After Eating OlivesGoldstein, David S. / Holmes, Courtney / Cherup, Jamie / Sharabi, Yehonatan et al. | 2018
- 38
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A Pilot Dose‐Finding Study of Etanercept in Rheumatoid ArthritisBreedveld, Ferdinand C. / Jones, Heather E. / Peifer, Kim / Korth‐Bradley, Joan et al. | 2018
- 46
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LY3127760, a Selective Prostaglandin E4 (EP4) Receptor Antagonist, and Celecoxib: A Comparison of Pharmacological ProfilesJin, Yan / Smith, Claire / Hu, Leijun / Coutant, David E. / Whitehurst, Kelly / Phipps, Krista / McNearney, Terry Ann / Yang, Xiao / Ackermann, Bradley / Pottanat, Thomas et al. | 2018
- 54
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Population Pharmacokinetics of Fosdagrocorat (PF‐04171327), a Dissociated Glucocorticoid Receptor Agonist, in Patients With Rheumatoid ArthritisWeatherley, Barry / McFadyen, Lynn / Tammara, Brinda et al. | 2018
- 63
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Dopamine Transporter Neuroimaging as an Enrichment Biomarker in Early Parkinson's Disease Clinical Trials: A Disease Progression Modeling AnalysisConrado, Daniela J. / Nicholas, Timothy / Tsai, Kuenhi / Macha, Sreeraj / Sinha, Vikram / Stone, Julie / Corrigan, Brian / Bani, Massimo / Muglia, Pierandrea / Watson, Ian A. et al. | 2018
- 71
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Patient Decisions to Receive Secondary Pharmacogenomic Findings and Development of a Multidisciplinary Practice Model to Integrate Results Into Patient CareHicks, J. Kevin / Shealy, Amy / Schreiber, Allison / Coleridge, Marissa / Noss, Ryan / Natowicz, Marvin / Moran, Rocio / Moss, Timothy / Erwin, Angelika / Eng, Charis et al. | 2018
- 77
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The Translational Science Benefits Model: A New Framework for Assessing the Health and Societal Benefits of Clinical and Translational SciencesLuke, Douglas A. / Sarli, Cathy C. / Suiter, Amy M. / Carothers, Bobbi J. / Combs, Todd B. / Allen, Jae L. / Beers, Courtney E. / Evanoff, Bradley A. et al. | 2018
- 85
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Electronic Health Record Phenotypes for Precision Medicine: Perspectives and Caveats From Treatment of Breast Cancer at a Single InstitutionBreitenstein, Matthew K. / Liu, Hongfang / Maxwell, Kara N. / Pathak, Jyotishman / Zhang, Rui et al. | 2018
- 93
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Erratum to “Phase I Studies of Acebilustat: Pharmacokinetics, Pharmacodynamics, Food Effect, and CYP3A Induction”| 2018