Integrase-defective Lentiviral Vectors as a Delivery Platform for Targeted Modification of Adenosine Deaminase Locus (English)
- New search for: Joglekar, A. V.
- New search for: Hollis, R. P.
- New search for: Kuftinec, G.
- New search for: Senadheera, S.
- New search for: Chan, R.
- New search for: Kohn, D. B.
- New search for: Joglekar, A. V.
- New search for: Hollis, R. P.
- New search for: Kuftinec, G.
- New search for: Senadheera, S.
- New search for: Chan, R.
- New search for: Kohn, D. B.
In:
MOLECULAR THERAPY
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21
, 9
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1705-1717
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2013
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ISSN:
- Article (Journal) / Print
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Title:Integrase-defective Lentiviral Vectors as a Delivery Platform for Targeted Modification of Adenosine Deaminase Locus
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Contributors:Joglekar, A. V. ( author ) / Hollis, R. P. ( author ) / Kuftinec, G. ( author ) / Senadheera, S. ( author ) / Chan, R. ( author ) / Kohn, D. B. ( author )
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Published in:MOLECULAR THERAPY ; 21, 9 ; 1705-1717
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Publisher:
- New search for: Elsevier Science B.V., Amsterdam
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Publication date:2013-01-01
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Size:13 pages
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ISSN:
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Type of media:Article (Journal)
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Type of material:Print
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Language:English
- New search for: 616.042
- Further information on Dewey Decimal Classification
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Classification:
DDC: 616.042 -
Source:
© Metadata Copyright the British Library Board and other contributors. All rights reserved.
Table of contents – Volume 21, Issue 9
The tables of contents are generated automatically and are based on the data records of the individual contributions available in the index of the TIB portal. The display of the Tables of Contents may therefore be incomplete.
- 1639
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How to Design a Cell or Gene Therapy Clinical Trial: Advice from the FDAGee, A. P. et al. | 2013
- 1642
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In This Issue| 2013
- 1643
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Research Highlights| 2013
- 1644
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The Evolution of Nonclinical Regulatory Science: Advanced Therapy Medicinal Products as a ParadigmVestergaard, Henrik Tang / Apote, Lucia D' / Schneider, Christian K / Herberts, Carla et al. | 2013
- 1648
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Covert Warfare Against the Immune System: Decoy Capsids, Stealth Genomes, and SuppressorsHoffman, B. E. / Herzog, R. W. et al. | 2013
- 1650
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Generating SM(a)RTer Compounds for Translation Termination Suppression in A-T and Other Genetic DisordersLavin, Martin F et al. | 2013
- 1653
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A New Series of Small Molecular Weight Compounds Induce Read Through of All Three Types of Nonsense Mutations in the ATM GeneDu, L. / Jung, M. E. / Damoiseaux, R. / Completo, G. / Fike, F. / Ku, J. M. / Nahas, S. / Piao, C. / Hu, H. / Gatti, R. A. et al. | 2013
- 1661
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Intrapleural Administration of AAV9 Improves Neural and Cardiorespiratory Function in Pompe DiseaseFalk, Darin J / Mah, Cathryn S / Soustek, Meghan S / Lee, Kun-Ze / ElMallah, Mai K / Cloutier, Denise A / Fuller, David D / Byrne, Barry J et al. | 2013
- 1668
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Disruption of TAB1/p38α Interaction Using a Cell-permeable Peptide Limits Myocardial Ischemia/Reperfusion InjuryWang, Q. / Feng, J. / Wang, J. / Zhang, X. / Zhang, D. / Zhu, T. / Wang, W. / Wang, X. / Jin, J. / Cao, J. et al. | 2013
- 1678
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TP53-independent Function of miR-34a via HDAC1 and p21CIP1/WAF1Zhao, J. / Lammers, P. / Torrance, C. J. / Bader, A. G. et al. | 2013
- 1687
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Ultrasound-targeted Microbubble Destruction-mediated Gene Delivery Into Canine LiversNoble, Misty L / Kuhr, Christian S / Graves, Scott S / Loeb, Keith R / Sun, Samuel S / Keilman, George W / Morrison, Kyle P / Paun, Marla / Storb, Rainer F / Miao, Carol H et al. | 2013
- 1695
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Targeted Gene Addition in Human Epithelial Stem Cells by Zinc-finger Nuclease-mediated Homologous RecombinationColuccio, A. / Miselli, F. / Lombardo, A. / Marconi, A. / Malagoli Tagliazucchi, G. / Goncalves, M. A. / Pincelli, C. / Maruggi, G. / Del Rio, M. / Naldini, L. et al. | 2013
- 1705
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Integrase-defective Lentiviral Vectors as a Delivery Platform for Targeted Modification of Adenosine Deaminase LocusJoglekar, A. V. / Hollis, R. P. / Kuftinec, G. / Senadheera, S. / Chan, R. / Kohn, D. B. et al. | 2013
- 1718
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Reading Frame Correction by Targeted Genome Editing Restores Dystrophin Expression in Cells From Duchenne Muscular Dystrophy PatientsOusterout, D. G. / Perez-Pinera, P. / Thakore, P. I. / Kabadi, A. M. / Brown, M. T. / Qin, X. / Fedrigo, O. / Mouly, V. / Tremblay, J. P. / Gersbach, C. A. et al. | 2013
- 1738
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Meganuclease-mediated Virus Self-cleavage Facilitates Tumor-specific Virus ReplicationGurlevik, E. / Schache, P. / Goez, A. / Kloos, A. / Woller, N. / Armbrecht, N. / Manns, M. P. / Kubicka, S. / Kuhnel, F. et al. | 2013
- 1749
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Suppression of Antiviral Innate Immunity by Sunitinib Enhances Oncolytic VirotherapyJha, Babal K / Dong, Beihua / Nguyen, Carvell T / Polyakova, Irina / Silverman, Robert H et al. | 2013
- 1758
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Endothelial Differentiation of Adipose Tissue-Derived Mesenchymal Stromal Cells in Glioma Tumors: Implications for Cell-Based TherapyBago, J. R. / Alieva, M. / Soler, C. / Rubio, N. / Blanco, J. et al. | 2013
- 1767
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Snail as a Potential Target Molecule in Cardiac Fibrosis: Paracrine Action of Endothelial Cells on Fibroblasts Through Snail and CTGF AxisLee, Sae-Won / Won, Joo-Yun / Kim, Woo Jean / Lee, Jaewon / Kim, Kyung-Hee / Youn, Seock-Won / Kim, Ju-Young / Lee, Eun Ju / Kim, Yong-Jin / Kim, Kyu-Won et al. | 2013
- 1778
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Third-party Mesenchymal Stem Cells Improved Human Islet Transplantation in a Humanized Diabetic Mouse ModelWu, Hao / Wen, Di / Mahato, Ram I et al. | 2013
- 1787
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The Novel Replication-defective Vaccinia Virus (Tiantan Strain)–based Hepatitis C Virus Vaccine Induces Robust Immunity in MacaquesWen, B. / Deng, Y. / Chen, H. / Guan, J. / Chuai, X. / Ruan, L. / Kong, W. / Tan, W. et al. | 2013
- 1796
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Therapeutic DNA Vaccination Using In Vivo Electroporation Followed by Standard of Care Therapy in Patients With Genotype 1 Chronic Hepatitis CWeiland, O. / Ahlen, G. / Diepolder, H. / Jung, M. C. / Levander, S. / Fons, M. / Mathiesen, I. / Sardesai, N. Y. / Vahlne, A. / Frelin, L. et al. | 2013
- e1
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Late Breaking Abstracts: Presented at the American Society of Gene & Cell Therapy's 16thAnnual Meeting, May 15–18, 2013, Salt Lake City, Utah| 2013
- e1
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Late Breaking Abstracts: Presented at the American Society of Gene & Cell Therapy’s 16thAnnual Meeting, May 15–18, 2013, Salt Lake City, Utah| 2013
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Modulation of CD8+ T cell responses to AAV vectors with IgG-derived MHC class II epitopesHui, D. J. / Basner-Tschakarjan, E. / Chen, Y. / Davidson, R. J. / Buchlis, G. / Yazicioglu, M. / Pien, G. C. / Finn, J. D. / Haurigot, V. / Tai, A. et al. | 2013