Characterization of Gene Alterations following Editing of the β-Globin Gene Locus in Hematopoietic Stem/Progenitor Cells (English)
- New search for: Long, Joseph
- New search for: Hoban, Megan D.
- New search for: Cooper, Aaron R.
- New search for: Kaufman, Michael L.
- New search for: Kuo, Caroline Y.
- New search for: Campo-Fernandez, Beatriz
- New search for: Lumaquin, Dianne
- New search for: Hollis, Roger P.
- New search for: Wang, Xiaoyan
- New search for: Kohn, Donald B.
- New search for: Romero, Zulema
- New search for: Long, Joseph
- New search for: Hoban, Megan D.
- New search for: Cooper, Aaron R.
- New search for: Kaufman, Michael L.
- New search for: Kuo, Caroline Y.
- New search for: Campo-Fernandez, Beatriz
- New search for: Lumaquin, Dianne
- New search for: Hollis, Roger P.
- New search for: Wang, Xiaoyan
- New search for: Kohn, Donald B.
- New search for: Romero, Zulema
In:
Molecular therapy
;
26
, 2
;
468-479
;
2018
-
ISSN:
- Article (Journal) / Print
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Title:Characterization of Gene Alterations following Editing of the β-Globin Gene Locus in Hematopoietic Stem/Progenitor Cells
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Contributors:Long, Joseph ( author ) / Hoban, Megan D. ( author ) / Cooper, Aaron R. ( author ) / Kaufman, Michael L. ( author ) / Kuo, Caroline Y. ( author ) / Campo-Fernandez, Beatriz ( author ) / Lumaquin, Dianne ( author ) / Hollis, Roger P. ( author ) / Wang, Xiaoyan ( author ) / Kohn, Donald B. ( author )
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Published in:Molecular therapy ; 26, 2 ; 468-479
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Publisher:
- New search for: Elsevier Science B.V., Amsterdam
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Publication date:2018-01-01
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Size:12 pages
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ISSN:
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Type of media:Article (Journal)
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Type of material:Print
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Language:English
- New search for: 615.89505
- Further information on Dewey Decimal Classification
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Classification:
DDC: 615.89505 -
Source:
© Metadata Copyright the British Library Board and other contributors. All rights reserved.
Table of contents – Volume 26, Issue 2
The tables of contents are generated automatically and are based on the data records of the individual contributions available in the index of the TIB portal. The display of the Tables of Contents may therefore be incomplete.
- 329
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Modeling Unique Patients in Humanized Mice: Toward a Curative Strategy for HIVDorner, Marcus / de Jong, Ype P. et al. | 2018
- 331
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In This Issue| 2018
- 332
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Research Highlights| 2018
- 334
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Boosting, Not Breaking: CRISPR Activators Treat Disease ModelsGemberling, Matthew / Gersbach, Charles A. et al. | 2018
- 336
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Taking a Hint from Structural Biology: To Better Understand AAV Transport across the BBBWang, Dan / Gao, Guangping et al. | 2018
- 338
-
Intraoperative Molecular Imaging in Lung Cancer: The State of the Art and the FutureRogalla, Stephan / Joosten, Sebastiaan C.M. / Alam, Israt S. / Gambhir, Sanjiv S. / Vermesh, Ophir et al. | 2018
- 342
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CAR-T Cells: A Systematic Review and Mixed Methods Analysis of the Clinical Trial LandscapePettitt, David / Arshad, Zeeshaan / Smith, James / Stanic, Tijana / Holländer, Georg / Brindley, David et al. | 2018
- 354
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Chimeric Antigen Receptor-Engineered Human Gamma Delta T Cells: Enhanced Cytotoxicity with Retention of Cross PresentationCapsomidis, Anna / Benthall, Gabriel / Van Acker, Heleen H. / Fisher, Jonathan / Kramer, Anne M. / Abeln, Zarah / Majani, Yvonne / Gileadi, Talia / Wallace, Rebecca / Gustafsson, Kenth et al. | 2018
- 366
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Development of GPC3-Specific Chimeric Antigen Receptor-Engineered Natural Killer Cells for the Treatment of Hepatocellular CarcinomaYu, Min / Luo, Hong / Fan, Mingliang / Wu, Xiuqi / Shi, Bizhi / Di, Shengmeng / Liu, Ying / Pan, Zeyan / Jiang, Hua / Li, Zonghai et al. | 2018
- 379
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An Efficient Single-Cell RNA-Seq Approach to Identify Neoantigen-Specific T Cell ReceptorsLu, Yong-Chen / Zheng, Zhili / Robbins, Paul F. / Tran, Eric / Prickett, Todd D. / Gartner, Jared J. / Li, Yong F. / Ray, Satyajit / Franco, Zulmarie / Bliskovsky, Valery et al. | 2018
- 390
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Identification of a Folate Receptor-Targeted Near-Infrared Molecular Contrast Agent to Localize Pulmonary AdenocarcinomasPredina, Jarrod D. / Newton, Andrew D. / Connolly, Courtney / Dunbar, Ashley / Baldassari, Michael / Deshpande, Charuhas / Cantu, Edward / Stadanlick, Jason / Kularatne, Sumith A. / Low, Philip S. et al. | 2018
- 404
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Irradiation Enhances Abscopal Anti-tumor Effects of Antigen-Specific Immunotherapy through Regulating Tumor MicroenvironmentChang, Ming-Cheng / Chen, Yu-Li / Lin, Han-Wei / Chiang, Ying-Cheng / Chang, Chi-Fang / Hsieh, Shu-Feng / Chen, Chi-An / Sun, Wei-Zen / Cheng, Wen-Fang et al. | 2018
- 420
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MRNA Vaccine with Antigen-Specific Checkpoint Blockade Induces an Enhanced Immune Response against Established MelanomaWang, Yuhua / Zhang, Lu / Xu, Zhenghong / Miao, Lei / Huang, Leaf et al. | 2018
- 435
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Synergy of Immune Checkpoint Blockade with a Novel Synthetic Consensus DNA Vaccine Targeting TERTDuperret, Elizabeth K. / Wise, Megan C. / Trautz, Aspen / Villarreal, Daniel O. / Ferraro, Bernadette / Walters, Jewell / Yan, Jian / Khan, Amir / Masteller, Emma / Humeau, Laurent et al. | 2018
- 446
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Self-Amplifying RNA Vaccines Give Equivalent Protection against Influenza to mRNA Vaccines but at Much Lower DosesVogel, Annette B. / Lambert, Laura / Kinnear, Ekaterina / Busse, David / Erbar, Stephanie / Reuter, Kerstin C. / Wicke, Lena / Perkovic, Mario / Beissert, Tim / Haas, Heinrich et al. | 2018
- 456
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Engineering Protein-Secreting Plasma Cells by Homology-Directed Repair in Primary Human B CellsHung, King L. / Meitlis, Iana / Hale, Malika / Chen, Chun-Yu / Singh, Swati / Jackson, Shaun W. / Miao, Carol H. / Khan, Iram F. / Rawlings, David J. / James, Richard G. et al. | 2018
- 468
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Characterization of Gene Alterations following Editing of the β-Globin Gene Locus in Hematopoietic Stem/Progenitor CellsLong, Joseph / Hoban, Megan D. / Cooper, Aaron R. / Kaufman, Michael L. / Kuo, Caroline Y. / Campo-Fernandez, Beatriz / Lumaquin, Dianne / Hollis, Roger P. / Wang, Xiaoyan / Kohn, Donald B. et al. | 2018
- 480
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Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-HemoglobinopathiesBhukhai, Kanit / de Dreuzy, Edouard / Giorgi, Marie / Colomb, Charlotte / Negre, Olivier / Denaro, Maria / Gillet-Legrand, Béatrix / Cheuzeville, Joëlle / Paulard, Anaïs / Trebeden-Negre, Hélène et al. | 2018
- 496
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Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic MiceBunting, Stuart / Zhang, Lening / Xie, Lin / Bullens, Sherry / Mahimkar, Rajeev / Fong, Sylvia / Sandza, Krystal / Harmon, Danielle / Yates, Bridget / Handyside, Britta et al. | 2018
- 510
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Mapping the Structural Determinants Required for AAVrh.10 Transport across the Blood-Brain BarrierAlbright, Blake H. / Storey, Claire M. / Murlidharan, Giridhar / Castellanos Rivera, Ruth M. / Berry, Garrett E. / Madigan, Victoria J. / Asokan, Aravind et al. | 2018
- 524
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Triple Vectors Expand AAV Transfer Capacity in the RetinaMaddalena, Andrea / Tornabene, Patrizia / Tiberi, Paola / Minopoli, Renato / Manfredi, Anna / Mutarelli, Margherita / Rossi, Settimio / Simonelli, Francesca / Naggert, Jurgen K. / Cacchiarelli, Davide et al. | 2018
- 542
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AAV8-antiVEGFfab Ocular Gene Transfer for Neovascular Age-Related Macular DegenerationLiu, Yuanyuan / Fortmann, Seth D. / Shen, Jikui / Wielechowski, Erik / Tretiakova, Anna / Yoo, Stephen / Kozarsky, Karen / Wang, Jiangxia / Wilson, James M. / Campochiaro, Peter A. et al. | 2018
- 550
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Selective α-Synuclein Knockdown in Monoamine Neurons by Intranasal Oligonucleotide Delivery: Potential Therapy for Parkinson’s DiseaseAlarcón-Arís, Diana / Recasens, Ariadna / Galofré, Mireia / Carballo-Carbajal, Iria / Zacchi, Nicolás / Ruiz-Bronchal, Esther / Pavia-Collado, Rubén / Chica, Rosario / Ferrés-Coy, Albert / Santos, Marina et al. | 2018
- 568
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Hypoxic Lung-Cancer-Derived Extracellular Vesicle MicroRNA-103a Increases the Oncogenic Effects of Macrophages by Targeting PTENHsu, Ya-Ling / Hung, Jen-Yu / Chang, Wei-An / Jian, Shu-Fang / Lin, Yi-Shiuan / Pan, Yi-Chung / Wu, Cheng-Ying / Kuo, Po-Lin et al. | 2018
- 582
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MiR-23b Suppresses Leukocyte Migration and Pathogenesis of Experimental Autoimmune Encephalomyelitis by Targeting CCL7Zhang, Yuan / Han, Juan-Juan / Liang, Xiao-Yan / Zhao, Li / Zhang, Fei / Rasouli, Javad / Wang, Zhe-Zhi / Zhang, Guang-Xian / Li, Xing et al. | 2018
- 593
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Global MicroRNA Profiling in Human Bone Marrow Skeletal—Stromal or Mesenchymal–Stem Cells Identified Candidates for Bone RegenerationChang, Chi-Chih / Venø, Morten T. / Chen, Li / Ditzel, Nicholas / Le, Dang Q.S. / Dillschneider, Philipp / Kassem, Moustapha / Kjems, Jørgen et al. | 2018
- 606
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Stem Cell Secretome and Its Effect on Cellular Mechanisms Relevant to Wound HealingPark, Se-Ra / Kim, Jae-Wan / Jun, Hee-Sook / Roh, Joo Young / Lee, Hwa-Yong / Hong, In-Sun et al. | 2018
- 618
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Skeletal Muscle Regenerative Potential of Human MuStem Cells following Transplantation into Injured Mice MuscleLorant, Judith / Saury, Charlotte / Schleder, Cindy / Robriquet, Florence / Lieubeau, Blandine / Négroni, Elisa / Leroux, Isabelle / Chabrand, Lucie / Viau, Sabrina / Babarit, Candice et al. | 2018
- 634
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The Impact of the CD9 Tetraspanin on Lentivirus Infectivity and Exosome SecretionBöker, Kai O. / Lemus-Diaz, Nicolas / Rinaldi Ferreira, Rafael / Schiller, Lara / Schneider, Stefan / Gruber, Jens et al. | 2018
- 648
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Cellular Uptake of A Taurine-Modified, Ester Bond-Decorated D-Peptide Derivative via Dynamin-Based Endocytosis and MacropinocytosisZhou, Jie / Du, Xuewen / Berciu, Cristina / Del Signore, Steven J. / Chen, Xiaoyi / Yamagata, Natsuko / Rodal, Avital A. / Nicastro, Daniela / Xu, Bing et al. | 2018